Nicolas Wein Center for Gene Therapy The Research Institute at Nationwide Children’s Hospital Biography Publications Institution JoVE Articles Nicolas Wein has not added a biography. If you are Nicolas Wein and would like to personalize this page please email our Author Liaison for assistance. Publications Lack of Toxicity in Non-human Primates Receiving Clinically Relevant Doses of an AAV9.U7snRNA Vector Designed to Induce DMD Exon 2 Skipping Human Gene Therapy. Jan, 2021 | Pubmed ID: 33406986 Personalized Gene and Cell Therapy for Duchenne Muscular Dystrophy Neuromuscular Disorders : NMD. 10, 2018 | Pubmed ID: 30224293 Dp412e: a Novel Human Embryonic Dystrophin Isoform Induced by BMP4 in Early Differentiated Cells Skeletal Muscle. 2015 | Pubmed ID: 26568816 The ZZ Domain of Dystrophin in DMD: Making Sense of Missense Mutations Human Mutation. Feb, 2014 | Pubmed ID: 24302611 Nöromüsküler Bozukluklar için Tedavileri Araştırmak için İnsan Fibroblastlarının Myoblastlara Doğrudan Yeniden Programlanması Camila F. Almeida1, Emma C. Frair1, Nianyuan Huang1, Reid Neinast2, Kim L. McBride2,3,4,6, Robert B. Weiss5, Kevin M. Flanigan1,6, Nicolas Wein1,6 1Center for Gene Therapy, The Research Institute at Nationwide Children’s Hospital, 2Center for Cardiovascular Research, The Research Institute at Nationwide Children’s Hospital, 3The Heart Center, Nationwide Children’s Hospital, 4Division of Genetic and Genomic Medicine, Nationwide Children’s Hospital, 5Department of Human Genetics, The University of Utah School of Medicine, 6Department of Pediatrics, The Ohio State University JoVE 61991 Genetics
Nöromüsküler Bozukluklar için Tedavileri Araştırmak için İnsan Fibroblastlarının Myoblastlara Doğrudan Yeniden Programlanması Camila F. Almeida1, Emma C. Frair1, Nianyuan Huang1, Reid Neinast2, Kim L. McBride2,3,4,6, Robert B. Weiss5, Kevin M. Flanigan1,6, Nicolas Wein1,6 1Center for Gene Therapy, The Research Institute at Nationwide Children’s Hospital, 2Center for Cardiovascular Research, The Research Institute at Nationwide Children’s Hospital, 3The Heart Center, Nationwide Children’s Hospital, 4Division of Genetic and Genomic Medicine, Nationwide Children’s Hospital, 5Department of Human Genetics, The University of Utah School of Medicine, 6Department of Pediatrics, The Ohio State University JoVE 61991 Genetics