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Education
Author Spotlight: Assessing Intrathecal Gene Therapy Efficacy in Juvenile Rats
制备试剂以递送腺相关血清型 9 载体
在幼鼠中通过腰椎穿刺递送基因治疗载体
描述了一种外科手术,用于向幼年大鼠的腰椎池进行注射。这种方法已被用于基因治疗载体的鞘内递送,但预计这种方法可用于多种疗法,包括细胞和药物。
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