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CRISPR/Cas9 teknologi i gjenopprette Dystrofingenet uttrykk i iPSC-avledet Muscle forfedre
 
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CRISPR/Cas9 teknologi i gjenopprette Dystrofingenet uttrykk i iPSC-avledet Muscle forfedre

Article DOI: 10.3791/59432-v 07:44 min September 14th, 2019
September 14th, 2019

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Her presenterer vi en Cas9-basert exon23 sletting protokoll for å gjenopprette dystrofingenet uttrykk i iPSC fra DMDMDX mus-avledet hud fibroblaster og direkte differensiere iPSCs til myogenic stamceller (MPC) ved hjelp av tet-on MyoD aktiveringssystem.

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Utviklingsbiologi indusert Pluripotent stamceller iPSC CRISPR/Cas9 DMD dystrofingenet myogenic stamfar differensiering
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